95% of kids with “bubble boy” disease cured by one-time gene therapy
95% of kids with “bubble boy” disease cured by one-time gene therapy
newatlas.com
95% of kids with “bubble boy” disease cured by one-time gene therapy
A new gene therapy using patients’ own stem cells has safely cured ADA-SCID — the “bubble boy” disease — in 95% of children, restoring full immune function.